Speaker Profile
Ph.D., Senior Vice President, Global Regulatory Affairs, Intellia Tx
Biography
Aron spearheads Intellia's efforts in developing groundbreaking gene editing products targeting patients with rare diseases.Prior to joining Intellia, Aron was the Vice President of Global Regulatory Affairs at Sangamo Therapeutics, Inc., where he led regulatory strategies for 3 years and 5 months. His tenure at Bavarian Nordic further exemplifies his expertise, where he was responsible for global regulatory strategies for vaccine programs in oncology and infectious diseases.Aron's deep experience in the industry is marked by his tenure at various leading pharmaceutical companies, including Pfizer, where he managed a wide range of therapeutic areas and oversaw key regulatory programs for drugs like VIAGRA, TIKOSYN, and NORVASC. His earlier work at DuPont Pharmaceuticals honed his skills in toxicology, emphasizing his comprehensive understanding of drug development and safety evaluation.
Session Abstract – PMWC 2024 Silicon Valley
Track Co-Chairs:
Yael Weiss, Mahzi Tx
Peter Marks, FDA
- PMWC 2024 Award Ceremony
Pioneer Honoree: Katherine A. High, AskBio
Pioneer Honoree: Timothy Yu, Boston Children's Hospital
- Piloting Interventional Genomics for Orphan Diseases
Keynote: Timothy Yu, Boston Children's Hospital
- Accelerated Approval for Small Populations: Biomarkers & Endpoints (PANEL)
Chair: Peter Marks, FDA
- Jennifer Puck, UCSF
- Maria Grazia Roncarolo, Tr1X
- Katherine A. High, Rockefeller University
- Jennifer Panagoulias, FAST (Angelman Syndrome Foundation)
- Timothy Yu, Boston Children's Hospital - Novel Clinical Design Approaches in Rare Diseases (PANEL)
Chair: Adam Shaywitz, Bridge Bio
- Salvador Rico, Encoded Therapeutics
- Eric Crombez, Ultragenyx
- Elizabeth Berri Kravis, Rush University
- Empowering Patient Advocacy in Rare Disease Therapies (PANEL)
Chair: Yael Weiss, Mahzi Tx
- Justin West, KCNT1 Foundation
- Michael Graglia, Syngap Research Fund
- Wendy Erler, Alexion Pharmaceuticals - Advancing the Frontier: Gene Editing for Rare Diseases (PANEL)
Chair: Matthew Porteus, Stanford
- James Chung, Kyverna Therapeutics
- Lucas Harrington, Mammoth Biosciences
- Aron Stein, Intellia Therapeutics - Advancing the Frontier: Gene and Cell Therapies for Rare Diseases (PANEL)
Chair: Morten Sogaard, Astellas Gene Therapies
- Pooja Agarwal, BioMarin Pharmaceutical
- David Kirn, 4dmt
- Adrian Veres, Dyno Therapeutics
- Thomas Wechsler, J&J
- PMWC Showcase
- Dominic Borie, Kyverna Therapeutics
